Gaucher and Pompe Diseases Enzyme Replacement Therapy (ERT) Market growth Underpinned Due to Increasing Incidences of Lysosomal Storage Disorders (LSD): FMI

Market players are relying on presenting novel technologies to advance efficient ERTs for several genetic conditions.

Future Market Insights, Dubai: The Gaucher and Pompe Disease ERT Market is anticipated to record a positive growth trajectory, despite facing a glitch in the initial months of COVID-19, due to rising orphan drug status designation to several drug candidates by the FDA. The market is further growing due to surge in a number of partnerships and collaborations among key market players.

“Increase in regulatory approvals by government authorities is leading the entrance of prominent enzyme replacement therapy providers, therefore making huge revenue prospects all over promising markets,” concludes the FMI analyst.

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Key Highlights

  • Europe to remain lucrative in the market, recording majority of the revenue share.
  • The type-1 Gaucher disease segment will record a significant growth pace amid the forecast period.
  • Parenteral administration remain highly preferred over oral route of administration.
  • Online pharmacies are likely to gain traction, growing at around 7% of CAGR during 2020-2030.


  • Rising incidences of lysosomal storage disorders (LSD), across the globe is driving the market growth.
  • Thriving orphan drug designations is anticipated to broaden the market scope over the assessment period.
  • Increasing prevalence of genetic disorders all over the world has boosted the growth in the market.


  • Alternative treatment approaches for more efficient treatment is anticipated to hamper the market growth.
  • Presence of the pathological and blood-brain barrier preconditions further prove to be hindrances for efficient adoption of ERT.

COVID-19 Impact on the Market

COVID-19 has severely impacted the worldwide healthcare sector. Regarding treatments and surgeries, key priority is inclining towards COVID-19 positive tested patients, bringing about postponement and delays of some procedures. This has further affected the Gaucher & Pompe Disease ERT market, registering a shortfall for hospital-based treatment. However, the slowdown didnt lasted for long, as government authorities leading healthcare providers to continue treatment for Type-3 and Type-1 Gaucher Disease patients.

Competitive Landscape

The Gaucher & Pompe Disease ERT market is characterised by the existence of a number of prominent pharmaceutical and healthcare corporations, focusing on path breaking technological advancements to present more efficient therapeutic solutions on account of strategic collaborations with several entities.

Key players identified in the market are Pfizer Inc., Tadeka Pharmaceuticals, BioMarin Pharmaceutical Inc., Merck KGaA Alexion Pharmaceuticals Inc., Janssen Pharmaceuticals Inc., Sanofi SA, Ultragenyx Pharmaceutical Inc., Shire PLC,AbbVie Inc., and Sigma-Tau Pharmaceuticals Inc.

About the Study

The study offers readers a comprehensive assessment of the Gaucher and Pompe Diseases Enzyme Replacement Therapy (ERT) Market. Global, regional and national-level analysis of the latest trends influencing the market is covered in this FMI report. The study provides insights on the basis of therapeutic condition (Gaucher disease and Pompe disease), route of administration (oral and parenteral) and distribution channel (hospital pharmacies, specialty treatment pharmacies, retail pharmacies and online pharmacies),  across key regions (North America, Latin America, Europe, China, Asia Pacific, Middle East & Africa).

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About Future Market Insights

Future Market Insights (FMI) is a leading provider of market intelligence and consulting services, serving clients in over 150 countries. FMI is headquartered in Dubai, the global financial capital, and has delivery centers in the U.S. and India. FMI’s latest market research reports and industry analysis help businesses navigate challenges and make critical decisions with confidence and clarity amidst breakneck competition. Our customized and syndicated market research reports deliver actionable insights that drive sustainable growth. A team of expert-led analysts at FMI continuously tracks emerging trends and events in a broad range of industries to ensure that our clients prepare for the evolving needs of their consumers.


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